European Journal of Pediatrics · 1975 · 77 citations · 10 references
Life SciencesGeneticsMolecular BiologyGene TherapyGenetic EngineeringMedical GeneticsGenetic DisordersArginase DeficiencyArgininosuccinate Lyase DeficiencyGene Replacement Constructs
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Gene Therapy for Human Genetic Disease?
Theodore Friedmann, Richard O. Roblin · Science · 1972 · 797 citations
ARGININÆMIA WITH ARGINASE DEFICIENCY
H. G. Terheggen, A. Schwenk, A. Löwenthal et al. · The Lancet · 1969 · 96 citations
Gene Therapy for Human Genetic Disease?
E. F. Neufeld, C. C. Sweeley, Sally J. Rogers et al. · Science · 1972 · 60 citations