Pharmaceutical Research · 2014 · 31 citations · 43 references
Life SciencesMolecular BiologyMolecular GeneticsGene ExpressionProtein EngineeringProtein SynthesisGene KnockoutZinc Finger DomainsZinc Finger MotifsZinc Finger Proteins
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Highly efficient endogenous human gene correction using designed zinc-finger nucleases
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