Design of Tissue-specific Regulatory Cassettes for High-level rAAV-mediated Expression in Skeletal and Cardiac Muscle

Maja Z. Salva, Charis L. Himeda, Phillip W.L. Tai, Eiko Nishiuchi, Paul Gregorevic, James M. Allen, Eric Finn, Quynh G Nguyen, Michael J. Blankinship, Leonard Meuse,

Molecular Therapy · 2007 · 226 citations · 47 references

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