Concepedia

Systemic delivery of genes to striated muscles using adeno-associated viral vectors

Paul Gregorevic, Michael J. Blankinship, James M. Allen, Robert W. Crawford, Leonard Meuse, Daniel G. Miller, David W. Russell, Jeffrey S. Chamberlain

Nature Medicine · 2004 · 611 citations · 31 references

DOIFull text

Open access

Concepts

References

31

Dystrophin protects the sarcolemma from stresses developed during muscle contraction.

Basil J. Petrof, Joseph B. Shrager, Hansell H. Stedman et al. · Proceedings of the National Academy of Sciences · 1993 · 1.5K citations

, , +17

Localized Igf-1 transgene expression sustains hypertrophy and regeneration in senescent skeletal muscle

Antonio Musarò, Karl J. A. McCullagh, Angelika Paul et al. · Nature Genetics · 2001 · 1.1K citations

, , +11

Increased microvascular permeability and endothelial fenestration induced by vascular endothelial growth factor

W. Gregory Roberts, George E. Palade · Journal of Cell Science · 1995 · 1K citations

, , +16

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B

Catherine S. Manno, Ah Keng Chew, S Hutchison et al. · Blood · 2003 · 747 citations · Full text

, , +11

Novel Tools for Production and Purification of Recombinant Adenoassociated Virus Vectors

Dirk Grimm, Andrea Kern, Karola Rittner et al. · Human Gene Therapy · 1998 · 700 citations

, , +16