Concepedia

Enzyme Replacement with Recombinant β-Glucuronidase in the Newborn Mucopolysaccharidosis Type VII Mouse

Carole Vogler, Mark S. Sands, A Higgins, Beth Levy, Jeffery Grubb, E H Birkenmeier, William S. Sly

Pediatric Research · 1993 · 100 citations · 5 references

DOI

Concepts

References

5

Therapeutic response to intravenous infusions of glucocerebrosidase in a patient with Gaucher disease.

Norman W. Barton, F S Furbish, Gary J. Murray et al. · Proceedings of the National Academy of Sciences · 1990 · 370 citations

, , +15

Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer

John H. Wolfe, Mark S. Sands, Jane E. Barker et al. · Nature · 1992 · 219 citations

, , +5

Proliferin secreted by cultured cells binds to mannose 6-phosphate receptors.

Sang Jun Lee, Daniel Nathans · Journal of Biological Chemistry · 1988 · 219 citations · Full text

, , +17

Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates.

Mark S. Sands, Jane E. Barker, Carole Vogler et al. · PubMed · 1993 · 163 citations

, , +6

Expression of the two mannose 6-phosphate receptors is spatially and temporally different during mouse embryogenesis

Ulrich Matzner, Kurt Von Figura, Regina Pohlmann · Development · 1992 · 58 citations · Full text

, , +14