Concepedia

U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping

Caroline Brun, Daniel M. Suter, Chantal Pauli, Patrick Dunant, Hanns Lochm�ller, Jean‐Marc Burgunder, D. Sch�mperli, Joachim Weis

Cellular and Molecular Life Sciences · 2003 · 65 citations · 29 references

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29

Dystrophin expression in the mdx mouse restored by stem cell transplantation

Emanuela Gussoni, Yuko Soneoka, Corinne D. Strickland et al. · Nature · 1999 · 1.8K citations

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Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

Sarah England, L. V. B. Nicholson, Mark Johnson et al. · Nature · 1990 · 604 citations

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Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Scott Q. Harper, Michael A. Hauser, Christiana DelloRusso et al. · Nature Medicine · 2002 · 561 citations

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Myoblast Transfer in the Treatment of Duchenne's Muscular Dystrophy

Jerry R. Mendell, John T. Kissel, Anthony A. Amato et al. · New England Journal of Medicine · 1995 · 522 citations · Full text

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Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in <i>mdx</i> mouse model

Bing Wang, Juan Li, Xiao Xiao · Proceedings of the National Academy of Sciences · 2000 · 497 citations

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