Publication | Open Access
Self-complementary AAV-mediated gene therapy restores cone function and prevents cone degeneration in two models of Rpe65 deficiency
69
Citations
44
References
2010
Year
Gene TherapiesAutoimmune DiseasePathogenesisImmunologyRpe65 DeficiencyAutoimmunityPrevents Cone DegenerationCone FunctionGene VectorMedicineCell BiologyCell SignalingNovel Therapy
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