Judith C. van Deutekom

Local Dystrophin Restoration with Antisense Oligonucleotide PRO051

Judith C. van Deutekom, Anneke A. M. Janson, Ieke B. Ginjaar et al. · New England Journal of Medicine · 2007 · 760 citations

Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy

Nathalie Goemans, M. Tulinius, Johanna T. van den Akker et al. · New England Journal of Medicine · 2011 · 659 citations · Full text

Comparative Analysis of Antisense Oligonucleotide Sequences for Targeted Skipping of Exon 51 During Dystrophin Pre-mRNA Splicing in Human Muscle

Virginia Arechavala‐Gomeza, Ian R. Graham, Linda Popplewell et al. · Human Gene Therapy · 2007 · 149 citations

Exon Skipping, Antisense Oligonucleotide Sequences, Duchenne Muscular Dystrophy +11

Preclinical PK and PD Studies on 2′-O-Methyl-phosphorothioate RNA Antisense Oligonucleotides in the mdx Mouse Model

Hans Heemskerk, Christa de Winter, Petra van Kuik et al. · Molecular Therapy · 2010 · 137 citations · Full text

Use of capillary Western immunoassay (Wes) for quantification of dystrophin levels in skeletal muscle of healthy controls and individuals with Becker and Duchenne muscular dystrophy

Chantal Beekman, Anneke A. M. Janson, Aabed Baghat et al. · PLoS ONE · 2018 · 129 citations · Full text

Muscle Function, Immunology, Muscle Physiology +19