Anneke A. M. Janson

Local Dystrophin Restoration with Antisense Oligonucleotide PRO051

Judith C. van Deutekom, Anneke A. M. Janson, Ieke B. Ginjaar et al. · New England Journal of Medicine · 2007 · 760 citations

Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy

Nathalie Goemans, M. Tulinius, Johanna T. van den Akker et al. · New England Journal of Medicine · 2011 · 659 citations · Full text

Antisense-Induced Multiexon Skipping for Duchenne Muscular Dystrophy Makes More Sense

Annemieke Aartsma‐Rus, Anneke A. M. Janson, Wendy E. Kaman et al. · The American Journal of Human Genetics · 2004 · 192 citations · Full text

Kinesiology, Degenerative Disease, Antisense-induced Multiexon Skipping +3

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy

Annemieke Aartsma‐Rus, Mattie Bremmer-Bout, Anneke A. M. Janson et al. · Neuromuscular Disorders · 2002 · 174 citations

Gene Therapies, Engineering, Mendelian Disorder +10

Guidelines for Antisense Oligonucleotide Design and Insight Into Splice-modulating Mechanisms

Annemieke Aartsma‐Rus, Laura Van de Vliet, Marscha Hirschi et al. · Molecular Therapy · 2008 · 145 citations · Full text