Mattie Bremmer-Bout

Local Dystrophin Restoration with Antisense Oligonucleotide PRO051

Judith C. van Deutekom, Anneke A. M. Janson, Ieke B. Ginjaar et al. · New England Journal of Medicine · 2007 · 762 citations

Medicine, Molecular Genetics, Molecular Medicine +15

Antisense-Induced Multiexon Skipping for Duchenne Muscular Dystrophy Makes More Sense

Annemieke Aartsma‐Rus, Anneke A. M. Janson, Wendy E. Kaman et al. · The American Journal of Human Genetics · 2004 · 193 citations · Full text

Medicine, Molecular Medicine, Gene Therapy +4

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy

Annemieke Aartsma‐Rus, Mattie Bremmer-Bout, Anneke A. M. Janson et al. · Neuromuscular Disorders · 2002 · 175 citations

Life Sciences, Genetics, Molecular Genetics +13

Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells

Annemieke Aartsma‐Rus, Wendy E. Kaman, Mattie Bremmer-Bout et al. · Gene Therapy · 2004 · 121 citations

Medicine, Molecular Biology, Molecular Genetics +13

Targeted Exon Skipping in Transgenic hDMD Mice: A Model for Direct Preclinical Screening of Human-Specific Antisense Oligonucleotides

Mattie Bremmer-Bout, Annemieke Aartsma‐Rus, Emile J. de Meijer et al. · Molecular Therapy · 2004 · 116 citations · Full text

Pharmacy, Molecular Biology, Molecular Medicine +17