J.C.T. van Deutekom

Development of Approaches to Improve Cell Survival in Myoblast Transfer Therapy

Zhuqing Qu, Levent Balkir, J.C.T. van Deutekom et al. · The Journal of Cell Biology · 1998 · 462 citations · Full text

Analysis of the tandem repeat locus D4Z4 associated with facioscapulohumeral muscular dystropothhy

Jane Hewitt, Robert Lyle, Lorraine N. Clark et al. · Human Molecular Genetics · 1994 · 322 citations

Biology, Rare Diseases, Repeat Sequences +15

Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

J.C.T. van Deutekom · Human Molecular Genetics · 2001 · 287 citations

Antisense-Induced Multiexon Skipping for Duchenne Muscular Dystrophy Makes More Sense

Annemieke Aartsma‐Rus, Anneke A. M. Janson, Wendy E. Kaman et al. · The American Journal of Human Genetics · 2004 · 192 citations · Full text

Kinesiology, Degenerative Disease, Antisense-induced Multiexon Skipping +3

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy

Annemieke Aartsma‐Rus, Mattie Bremmer-Bout, Anneke A. M. Janson et al. · Neuromuscular Disorders · 2002 · 174 citations

Gene Therapies, Engineering, Mendelian Disorder +10