Steven E. Raper

Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer

Steven E. Raper, Narendra Chirmule, Frank S. Lee et al. · Molecular Genetics and Metabolism · 2003 · 1.5K citations

Inflammation, Autoimmune Disease, Disease Mechanism +9

Recombinant adeno-associated virus for muscle directed gene therapy

Krishna J. Fisher, Karin Jooss, J. M. Alston et al. · Nature Medicine · 1997 · 654 citations

Virus Gene, Gene Vector, Biomedical Engineering +1

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia

Mariann Grossman, Steven E. Raper, Karen Kozarsky et al. · Nature Genetics · 1994 · 565 citations

Metabolic Syndrome, Gene Therapies, Hepatology +13

A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia

Mariann Grossman, Daniel J. Rader, David W.M. Muller et al. · Nature Medicine · 1995 · 534 citations

Lipid Disorder, Homozygous Familial Hypercholesterolaemia, Engineering +9

A Pilot Study of <i>In Vivo</i> Liver-Directed Gene Transfer with an Adenoviral Vector in Partial Ornithine Transcarbamylase Deficiency

Steven E. Raper, Marc Yudkoff, Narendra Chirmule et al. · Human Gene Therapy · 2002 · 350 citations