Mariann Grossman

A Controlled Study of Adenoviral-Vector–Mediated Gene Transfer in the Nasal Epithelium of Patients with Cystic Fibrosis

Michael R. Knowles, Kathy Hohneker, Zhaoqing Zhou et al. · New England Journal of Medicine · 1995 · 568 citations · Full text

Pharmacy, Genetics, Molecular Biology +17

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia

Mariann Grossman, Steven E. Raper, Karen Kozarsky et al. · Nature Genetics · 1994 · 565 citations

Medicine, Biotechnology, Molecular Biology +14

A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia

Mariann Grossman, Daniel J. Rader, David W.M. Muller et al. · Nature Medicine · 1995 · 534 citations

Life Sciences, Biotechnology, Genetics +15

Long-Term Improvement of Hypercholesterolemia After Ex Vivo Gene Therapy in LDLR-Deficient Rabbits

Jayanta Roy Chowdhury, Mariann Grossman, Sanjeev Gupta et al. · Science · 1991 · 369 citations

Medicine, Genetics, Molecular Medicine +17

Receptor-mediated gene delivery in vivo. Partial correction of genetic analbuminemia in Nagase rats

George Y. Wu, James M. Wilson, Fouad Shalaby et al. · Journal of Biological Chemistry · 1991 · 344 citations · Full text

Pharmacy, Molecular Biology, Molecular Genetics +17