Concepedia

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia

Mariann Grossman, Steven E. Raper, Karen Kozarsky, Evan A. Stein, John F. Engelhardt, David W.M. Muller, Paul J. Lupien, James M. Wilson

Nature Genetics · 1994 · 565 citations · 16 references

DOI

Concepts

References

16

Submucosal glands are the predominant site of CFTR expression in the human bronchus

John F. Engelhardt, James R. Yankaskas, Stephen A. Ernst et al. · Nature Genetics · 1992 · 649 citations

, , +13

Increased Expression of DNA Cointroduced with Nuclear Protein in Adult Rat Liver

Yasufumi Kaneda, Kunimitsu Iwai, Tsuyoshi Uchida · Science · 1989 · 456 citations

, , +16

Adenovirus–mediated in vivo gene transfer and expression in normal rat liver

Howard Jaffe, Claire Danel, Glenn Longenecker et al. · Nature Genetics · 1992 · 449 citations

, , +15

Liver Transplantation to Provide Low-Density-Lipoprotein Receptors and Lower Plasma Cholesterol in a Child with Homozygous Familial Hypercholesterolemia

David W. Bilheimer, Joseph L. Goldstein, Scott M. Grundy et al. · New England Journal of Medicine · 1984 · 446 citations · Full text

, , +16

HEART-LIVER TRANSPLANTATION IN A PATIENT WITH FAMILIAL HYPERCHOLESTEROLAEMIA

Thomas E. Starzl, Henry T. Bahnson, Robert L. Hardesty et al. · The Lancet · 1984 · 375 citations

, , +8