Luca Maggioni

Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy

Virginia Haurigot, Sara Marcó, Albert Ribera et al. · Journal of Clinical Investigation · 2013 · 231 citations · Full text

Medicine, Neurology, Neuroscience +17

CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)

Sandra Motas, Virginia Haurigot, Sara Marcó et al. · JCI Insight · 2016 · 61 citations · Full text

Pharmacy, Neurology, Neuroscience +17

Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy

Albert Ribera, Virginia Haurigot, Sara Marcó et al. · Human Molecular Genetics · 2014 · 53 citations · Full text

Life Sciences, Neurology, Neuroscience +14

Long-Term Efficacy and Safety of Insulin and Glucokinase Gene Therapy for Diabetes: 8-Year Follow-Up in Dogs

Maria Luisa Jaén, Laia Vilà, Ivet Elias et al. · Molecular Therapy — Methods & Clinical Development · 2017 · 50 citations · Full text

Medicine, Molecular Medicine, Veterinary Clinical Sciences +12