FGF21 gene therapy as treatment for obesity and insulin resistance

Verónica Jiménez, Claudia Jambrina, Estefanía Casana, +21

EMBO Molecular Medicine

Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy

Virginia Haurigot, Sara Marcó, Albert Ribera, +16

Journal of Clinical Investigation

ImmunologyExperimental PathologyPathologyTranslational MedicineMps Iiia +14

Sexual transmission of hepatitis C virus and its relation with hepatitis B virus and HIV.

Tor J, Josep M. Llibre, M. Moreno Carbonell, +6

BMJ

Correction of Pathological Accumulation of Glycosaminoglycans in Central Nervous System and Peripheral Tissues of MPSIIIA Mice Through Systemic AAV9 Gene Transfer

Albert Ruzo, Sara Marcó, Miquel García, +7

Human Gene Therapy

Aav9 Gene TransferImmunologyPathologyPeripheral NervesMucopolysaccharidosis Type Iiia +15

In Vivo Adeno-Associated Viral Vector–Mediated Genetic Engineering of White and Brown Adipose Tissue in Adult Mice

Verónica Jiménez, Sergio Muñoz, Estefanía Casana, +7

Diabetes

Metabolic RemodelingInsulin SignalingObesityMetabolic SyndromeCell Signaling +18

Long-Term Retinal PEDF Overexpression Prevents Neovascularization in a Murine Adult Model of Retinopathy

Virginia Haurigot, Pilar Villacampa, Albert Ribera, +4

PLoS ONE

Diabetic RetinopathyOcular DiseaseRetinaOphthalmologyExperimental Ophthalmology +13

Increased Intraocular Insulin-like Growth Factor-I Triggers Blood-Retinal Barrier Breakdown

Virginia Haurigot, Pilar Villacampa, Albert Ribera, +9

Journal of Biological Chemistry

CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)

Sandra Motas, Virginia Haurigot, Miquel García, +11

JCI Insight

Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy

Albert Ribera, Virginia Haurigot, Miquel García, +15

Human Molecular Genetics

NeurogenomicsImmunologyPathologyNeurochemical BiomarkersSynaptic Signaling +24

Liver Production of Sulfamidase Reverses Peripheral and Ameliorates CNS Pathology in Mucopolysaccharidosis IIIA Mice

Albert Ruzo, Miquel García, Albert Ribera, +10

Molecular Therapy