Sara Marcó

FGF21 gene therapy as treatment for obesity and insulin resistance

Verónica Jiménez, Claudia Jambrina, Estefanía Casana et al. · EMBO Molecular Medicine · 2018 · 329 citations · Full text

Life Sciences, Biochemistry, Biotechnology +17

Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy

Virginia Haurigot, Sara Marcó, Albert Ribera et al. · Journal of Clinical Investigation · 2013 · 231 citations · Full text

Medicine, Neurology, Neuroscience +17

Correction of Pathological Accumulation of Glycosaminoglycans in Central Nervous System and Peripheral Tissues of MPSIIIA Mice Through Systemic AAV9 Gene Transfer

Albert Ruzo, Sara Marcó, Miquel García et al. · Human Gene Therapy · 2012 · 104 citations · Full text

Medicine, Genetics, Neurology +15

CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)

Sandra Motas, Virginia Haurigot, Sara Marcó et al. · JCI Insight · 2016 · 61 citations · Full text

Pharmacy, Neurology, Neuroscience +17

Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy

Albert Ribera, Virginia Haurigot, Sara Marcó et al. · Human Molecular Genetics · 2014 · 53 citations · Full text

Life Sciences, Neurology, Neuroscience +14