Sandra Motas

FGF21 gene therapy as treatment for obesity and insulin resistance

Verónica Jiménez, Claudia Jambrina, Estefanía Casana et al. · EMBO Molecular Medicine · 2018 · 320 citations · Full text

Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy

Virginia Haurigot, Sara Marcó, Albert Ribera et al. · Journal of Clinical Investigation · 2013 · 229 citations · Full text

Immunology, Experimental Pathology, Pathology +16

CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)

Sandra Motas, Virginia Haurigot, Miquel García et al. · JCI Insight · 2016 · 61 citations · Full text

Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy

Albert Ribera, Virginia Haurigot, Miquel García et al. · Human Molecular Genetics · 2014 · 53 citations · Full text

Neurogenomics, Immunology, Pathology +26

Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID

Carles Roca, Sandra Motas, Sara Marcó et al. · Human Molecular Genetics · 2017 · 49 citations · Full text

In Vivo Gene Therapy, Human Mpsiiid, Immunodeficiencies +20