Joel D. Bohning

Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

Christopher E. Nelson, Yaoying Wu, Matthew Gemberling et al. · Nature Medicine · 2019 · 429 citations

Life Sciences, Genetics, Molecular Genetics +16

Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy

Adrian Pickar‐Oliver, Veronica Gough, Joel D. Bohning et al. · Molecular Therapy · 2021 · 67 citations · Full text

Life Sciences, Genetics, Molecular Biology +17

In Vivo Gene Editing of Muscle Stem Cells with Adeno-Associated Viral Vectors in a Mouse Model of Duchenne Muscular Dystrophy

Jennifer B. Kwon, Adarsh R. Ettyreddy, Ashish Vankara et al. · Molecular Therapy — Methods & Clinical Development · 2020 · 57 citations · Full text

Life Sciences, Biotechnology, Molecular Biology +16

Myogenic Progenitor Cell Lineage Specification by CRISPR/Cas9-Based Transcriptional Activators

Jennifer B. Kwon, Ashish Vankara, Adarsh R. Ettyreddy et al. · Stem Cell Reports · 2020 · 25 citations · Full text

Life Sciences, Developmental Biology, Molecular Biology +17