Fraser J. Wilkes

Stable gene transfer to the nervous system using a non-primate lentiviral vector

K Mitrophanous, Seonwoo Yoon, Jonathan B. Rohll et al. · Gene Therapy · 1999 · 282 citations

Xenotransplantation, Non-primate Lentiviral Vector, Stable Gene Transfer +9

Lentivector-mediated SMN replacement in a mouse model of spinal muscular atrophy

Mimoun Azzouz, Thanh T. Le, G. Ralph et al. · Journal of Clinical Investigation · 2004 · 198 citations · Full text

Immunology, Viral Pathogenesis, Sma Type 1 +16

Daily Treatment with SMTC1100, a Novel Small Molecule Utrophin Upregulator, Dramatically Reduces the Dystrophic Symptoms in the mdx Mouse

Jonathon M. Tinsley, Rebecca J. Fairclough, Richard Storer et al. · PLoS ONE · 2011 · 172 citations · Full text

Transduction Patterns of Pseudotyped Lentiviral Vectors in the Nervous System

Liang‐Fong Wong, Mimoun Azzouz, Lucy E. Walmsley et al. · Molecular Therapy · 2003 · 145 citations · Full text

Discovery of 2-Arylbenzoxazoles as Upregulators of Utrophin Production for the Treatment of Duchenne Muscular Dystrophy

Daniel Chancellor, Kay E. Davies, Olivier De Moor et al. · Journal of Medicinal Chemistry · 2011 · 75 citations

Medicinal Chemistry, Biochemistry, Duchenne Muscular Dystrophy +13