Thanh T. Le

RETRACTED ARTICLE: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN

Kevin D. Foust, Xueyong Wang, Vicki L. McGovern et al. · Nature Biotechnology · 2010 · 690 citations · Full text

Medicine, Neurobiology, Neuroscience +10

SMNΔ7, the major product of the centromeric survival motor neuron (SMN2) gene, extends survival in mice with spinal muscular atrophy and associates with full-length SMN

Thanh T. Le, Lan T. Pham, Matthew E.R. Butchbach et al. · Human Molecular Genetics · 2005 · 601 citations · Full text

Life Sciences, Genetics, Neuroscience +16

SMN oligomerization defect correlates with spinal muscular atrophy severity

Christian L. Lorson, John Strasswimmer, Jun-Mei Yao et al. · Nature Genetics · 1998 · 495 citations

Medicine, Neurology, Neuroscience +10

Lentivector-mediated SMN replacement in a mouse model of spinal muscular atrophy

Mimoun Azzouz, Thanh T. Le, G. Ralph et al. · Journal of Clinical Investigation · 2004 · 199 citations · Full text

Medicine, Neurology, Neuroscience +17

A transgene carrying an A2G missense mutation in the SMN gene modulates phenotypic severity in mice with severe (type I) spinal muscular atrophy

Umrao R. Monani, Matthew Pastore, Tatiana Gavrilina et al. · The Journal of Cell Biology · 2003 · 151 citations · Full text

Life Sciences, Genetics, Molecular Genetics +17