Lamya S. Shihabuddin

Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis

Holly Kordasiewicz, Lisa M. Stanek, Edward V. Wancewicz et al. · Neuron · 2012 · 758 citations · Full text

Knockout Mouse, Molecular Biology, Degenerative Disease +7

Adult Spinal Cord Stem Cells Generate Neurons after Transplantation in the Adult Dentate Gyrus

Lamya S. Shihabuddin, Philip J. Horner, Jasodhara Ray et al. · Journal of Neuroscience · 2000 · 704 citations · Full text

Adult Stem Cell, Neurodevelopment, Cellular Neurobiology +20

Antisense Oligonucleotides Delivered to the Mouse CNS Ameliorate Symptoms of Severe Spinal Muscular Atrophy

Marco A. Passini, Jie Bu, Amy M. Richards et al. · Science Translational Medicine · 2011 · 548 citations · Full text

iPSC-derived neurons from GBA1-associated Parkinson’s disease patients show autophagic defects and impaired calcium homeostasis

David C. Schöndorf, Massimo Aureli, Fiona E. McAllister et al. · Nature Communications · 2014 · 533 citations · Full text

Neurodegenerative Diseases, Neurobiology Of Disease, Molecular Neuroscience +14

CNS expression of glucocerebrosidase corrects α-synuclein pathology and memory in a mouse model of Gaucher-related synucleinopathy

S. Pablo Sardi, Jennifer Clarke, Cathrine Kinnecom et al. · Proceedings of the National Academy of Sciences · 2011 · 316 citations

Cns Expression, Synaptic Signaling, Social Sciences +16