Concepedia

Marco A. Passini

MA

Statistics

Publications

47

Citations

5.7K

H-Index

38

Active since

1997

Affiliations

Children's Hospital of Philadelphia(Current)

University of Pennsylvania

SynZyme Technologies (United States)

Icahn School of Medicine at Mount Sinai

Stony Brook University

Marco A. Passini is an author at Children's Hospital of Philadelphia specializing in neuroscience, life sciences, and molecular neuroscience.

Publications per year

1997–2022

47

Publications

47

Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model

Yimin Hua, Kentaro Sahashi, Gene Hung et al. · Genes & Development · 2010 · 655 citations · Full text

, , +17

Antisense Oligonucleotides Delivered to the Mouse CNS Ameliorate Symptoms of Severe Spinal Muscular Atrophy

Marco A. Passini, Jie Bu, Amy M. Richards et al. · Science Translational Medicine · 2011 · 553 citations · Full text

, , +12

CNS expression of glucocerebrosidase corrects α-synuclein pathology and memory in a mouse model of Gaucher-related synucleinopathy

S. Pablo Sardi, Jennifer Clarke, Cathrine Kinnecom et al. · Proceedings of the National Academy of Sciences · 2011 · 317 citations

, , +17

CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy

Marco A. Passini, Jie Bu, Eric M. Roskelley et al. · Journal of Clinical Investigation · 2010 · 295 citations · Full text

, , +17

Augmenting CNS glucocerebrosidase activity as a therapeutic strategy for parkinsonism and other Gaucher-related synucleinopathies

S. Pablo Sardi, Jennifer Clarke, Catherine Viel et al. · Proceedings of the National Academy of Sciences · 2013 · 247 citations · Full text

, , +17

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