Pablo Pérez‐Piñera

RNA-guided gene activation by CRISPR-Cas9–based transcription factors

Pablo Pérez‐Piñera, D. Dewran Koçak, Christopher M. Vockley et al. · Nature Methods · 2013 · 1.3K citations · Full text

Transcriptional Regulation, Natural Sciences, Molecular Biology +6

Multiplexed and Programmable Regulation of Gene Networks with an Integrated RNA and CRISPR/Cas Toolkit in Human Cells

Lior Nissim, Samuel D. Perli, Alexandra Fridkin et al. · Molecular Cell · 2014 · 449 citations · Full text

Gene Therapies, Functional Genomics, Gene Networks +14

Synergistic and tunable human gene activation by combinations of synthetic transcription factors

Pablo Pérez‐Piñera, David G. Ousterout, Jonathan M. Brunger et al. · Nature Methods · 2013 · 238 citations

Transcriptional Regulation, Transcription Factors, Natural Sciences +14

CRISPR-SKIP: programmable gene splicing with single base editors

Michael Gapinske, Alan Luu, Jackson Winter et al. · Genome biology · 2018 · 188 citations · Full text

Engineering, Genetics, Rna Splicing +17

Reading Frame Correction by Targeted Genome Editing Restores Dystrophin Expression in Cells From Duchenne Muscular Dystrophy Patients

David G. Ousterout, Pablo Pérez‐Piñera, Pratiksha I. Thakore et al. · Molecular Therapy · 2013 · 174 citations · Full text

Genetics, Molecular Biology, Disease Gene Identification +17