miRNA-embedded shRNAs for Lineage-specific BCL11A Knockdown and Hemoglobin F Induction

Swaroopa Guda, Christian Brendel, Raffaele Renella, Peng Du, Daniel E. Bauer, Matthew C. Canver, Jennifer K. Grenier, Andrew Grimson, Sophia C. Kamran, James E. Thornton,

Molecular Therapy · 2015 · 119 citations · 43 references

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