Concepedia

Suppression of rds Expression by siRNA and Gene Replacement Strategies for Gene Therapy Using rAAV Vector

Hilda Petrs‐Silva, Douglas Yasumura, Michael T. Matthes, Matthew M. LaVail, Alfred S. Lewin, William W. Hauswirth

Advances in experimental medicine and biology · 2011 · 30 citations · 9 references

DOI

Concepts

References

9

An RNA-directed nuclease mediates post-transcriptional gene silencing in Drosophila cells

Scott M. Hammond, Emily Bernstein, David Beach et al. · Nature · 2000 · 3K citations

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Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectors

Sergei Zolotukhin, Mark Potter, Irene Zolotukhin et al. · Methods · 2002 · 577 citations

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Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy

Robin R. Ali, Gian‐Marco Sarra, Mahesh de Alwis et al. · Nature Genetics · 2000 · 308 citations

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Gene replacement therapy in the retinal degeneration slow (rds)mouse: the effect on retinal degeneration following partial transduction of the retina

Gian‐Marco Sarra · Human Molecular Genetics · 2001 · 129 citations · Full text

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Subretinal injections in rodent eyes: effects on electrophysiology and histology of rat retina.

Adrian M. Timmers, Hong Zhang, A. Squitieri et al. · PubMed · 2001 · 113 citations

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