High-dose systemic adeno-associated virus vector administration causes liver and sinusoidal endothelial cell injury

Juliette Hordeaux, Jason Lamontagne, Chunjuan Song, George Buchlis, Cecilia Dyer, Elizabeth L. Buza, Ali Ramezani, Erik Wielechowski, Jenny A. Greig, Jessica A. Chichester,

Molecular Therapy · 2024 · 68 citations · 34 references

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