Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial - Concepedia

Concepedia

Publication | Open Access

Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial

DOI Full Paper Access

99

Citations

32

References

2023

Year

Perry B. Shieh, Nancy L. Kuntz, James J. Dowling, Wolfgang Müller‐Felber, Carsten G. Bönnemann, A. Seferian, Laurent Servais, Barbara K. Smith, Francesco Muntoni, Astrid Blaschek,

The Lancet Neurology

Abstract

Astellas Gene Therapies.

References

	Year	Citations

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