Publication | Open Access

Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial

Ocular DiseaseRetinaOphthalmologyExperimental OphthalmologyVoretigene NeparvovecInherited Retinal DystrophyGlaucomaRetinal TherapiesMedicine