Publication | Open Access
Targeted pseudouridylation: An approach for suppressing nonsense mutations in disease genes
65
Citations
51
References
2023
Year
Somatic VariantNovel TherapyNatural SciencesGeneticsMolecular BiologyNonsense MutationsAntisense TherapyDisease Gene IdentificationDisease GenesGene ExpressionMedicineGenome Editing
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