Gerard Platenburg

Local Dystrophin Restoration with Antisense Oligonucleotide PRO051

Judith C. van Deutekom, Anneke A. M. Janson, Ieke B. Ginjaar et al. · New England Journal of Medicine · 2007 · 762 citations

Medicine, Molecular Genetics, Molecular Medicine +15

Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy

Nathalie Goemans, M. Tulinius, Johanna T. van den Akker et al. · New England Journal of Medicine · 2011 · 665 citations · Full text

Medicine, Neurology, Neuromuscular Disorders +7

Generation Of Transgenic Dairy Cattle Using ‘in vitro’ Embryo Production

Paul Krimpenfort, Adriana Rademakers, Will Eyestone et al. · Nature Biotechnology · 1991 · 274 citations

Agriculture, Biotechnology, Dairy Science +14

Triplet-repeat oligonucleotide-mediated reversal of RNA toxicity in myotonic dystrophy

Susan Mulders, Walther J. A. A. van den Broek, Thurman M. Wheeler et al. · Proceedings of the National Academy of Sciences · 2009 · 250 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +17

Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect

Artur V. Cideciyan, Samuel G. Jacobson, Arlene V. Drack et al. · Nature Medicine · 2018 · 216 citations · Full text

Medicine, Ophthalmology, Vision Science +15