Concepedia

Expression of Amyloidogenic Transthyretin Drives Hepatic Proteostasis Remodeling in an Induced Pluripotent Stem Cell Model of Systemic Amyloid Disease

Richard M. Giadone, Derek C. Liberti, Taylor Matte, Jessica D. Rosarda, Celia Torres-Arancivia, Sabrina Ghosh, Jolene K. Diedrich, Sandra Pankow, Nicholas Skvir, Jenny Jean,

Stem Cell Reports · 2020 · 24 citations · 46 references

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References

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Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

David Adams, Alejandra González‐Duarte, William O’Riordan et al. · New England Journal of Medicine · 2018 · 2.8K citations · Full text

Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy

Jeffrey H. Schwartz, Balarama Gundapaneni, Perry Elliott et al. · New England Journal of Medicine · 2018 · 2.6K citations · Full text

Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis

Merrill D. Benson, Márcia Waddington‐Cruz, John L. Berk et al. · New England Journal of Medicine · 2018 · 1.4K citations · Full text

Repurposing Diflunisal for Familial Amyloid Polyneuropathy

John L. Berk, Ole B. Suhr, Laura Obici et al. · JAMA · 2013 · 679 citations · Full text

Quantitative evaluation of congo red binding to amyloid-like proteins with a beta-pleated sheet conformation.

William E. Klunk, Jay W. Pettegrew, Donald J. Abraham · Journal of Histochemistry & Cytochemistry · 1989 · 618 citations · Full text

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