Nature Medicine · 2020 · 53 citations · 53 references
Life SciencesGeneticsMolecular BiologyGene TherapyOligonucleotide ChemistryOligonucleotide DeliveryRna InterferenceAntisense Oligonucleotide DesignAntisense RnasOligonucleotide TherapeuticsOligonucleotide-mediated Gene TargetingTherapeutic Efficacy AssessmentTransgenic Mouse Models
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