Therapeutic efficacy of antisense oligonucleotides in mouse models of CLN3 Batten disease

Jessica L. Centa, Francine M. Jodelka, Anthony J. Hinrich, Tyler B. Johnson, Joseph Ochaba, Michaela Jackson, Dominik M. Duelli, Jill M. Weimer, Frank Rigo, Michelle L. Hastings

Nature Medicine · 2020 · 53 citations · 53 references

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