Publication | Open Access
Therapeutic efficacy of antisense oligonucleotides in mouse models of CLN3 Batten disease
52
Citations
53
References
2020
Year
Knockout MouseNovel TherapyCln3 Batten DiseaseMolecular BiologyTherapeutic EfficacyOligonucleotideAntisense OligonucleotidesAntisense TherapyImmunotherapyMedicineCell BiologyGenome Editing
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