Brain Research · 2019 · 25 citations · 52 references
Life SciencesGeneticsMolecular BiologyGenome EditingGenomicsNeurogeneticsAmyotrophic Lateral SclerosisCrispr-cas SystemsNeurodegenerative Disease GeneticsNeurodegenerative DiseasesNeurodegenerative DisordersSynthetic LethalityCrispr-based Lethality ScreensCrispr-based Synthetic Lethality ScreeningCrispr-cas9 Genome EditingCrispr-cas9 KnockoutGenome-wide Crispr Screening
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Genome-Scale CRISPR-Cas9 Knockout Screening in Human Cells
Ophir Shalem, Neville E. Sanjana, Ella Hartenian et al. · Science · 2013 · 5.5K citations · Full text
A Hexanucleotide Repeat Expansion in C9ORF72 Is the Cause of Chromosome 9p21-Linked ALS-FTD
Alan E. Renton, Elisa Majounie, Adrian J. Waite et al. · Neuron · 2011 · 4.5K citations · Full text
Genome-Scale CRISPR-Mediated Control of Gene Repression and Activation
Luke A. Gilbert, Max A. Horlbeck, Britt Adamson et al. · Cell · 2014 · 2.9K citations · Full text