Molecular Therapy — Methods & Clinical Development · 2019 · 53 citations · 44 references
MedicineGeneticsOphthalmologyGene TherapyOcular DiseaseRegenerative MedicineOcular Gene DeliveryOcular Gene TherapyPhotoreceptor DifferentiationRetinal DegenerationRetinal Pigment EpitheliumAdeno-associated Viral VectorsGene Therapy VectorsIncomplete PenetranceInduced Pluripotent Stem Cell ModelsInduced Pluripotent Stem CellsPhotoreceptor CellsRetinal Pigment Epithelium DegenerationRetinitis Pigmentosa Therapy
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Medicine, Genetics, Ophthalmology +17