Publication | Open Access
Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models
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Citations
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References
2018
Year
G Lca10 ModelsTranscriptional RegulationNatural SciencesGeneticsGene StructureMolecular BiologyHuman C.2991+1655aGene ExpressionMedicineSplicing VariantRna Processing
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