Effect of Genome Size on AAV Vector Packaging

Zhijian Wu, Hongyan Yang, Peter Colosi

Molecular Therapy

Viral ReplicationAav Vector GenomesVector GenomesGeneticsMolecular Biology +15

Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

Paul Kessler, Gregory M. Podsakoff, Xiaojuan Chen, +5

Proceedings of the National Academy of Sciences

Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery

Catherine A. Cukras, Henry E. Wiley, Brett G. Jeffrey, +15

Molecular Therapy

Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy

Dirk Grimm, Shangzhen Zhou, Hiroyuki Nakai, +11

Blood

Mutations on the External Surfaces of Adeno-AssociatedVirus Type 2 Capsids That Affect Transduction andNeutralization

Michael A. Lochrie, Gwen Tatsuno, Brian R. Christie, +5

Journal of Virology

Virus StructureMurine Monoclonal AntibodyMedicineExternal SurfacesPathogenesis +11

Adeno-Associated Viral Vector-Mediated Gene Transfer of Human Blood Coagulation Factor IX Into Mouse Liver

Hiroyuki Nakai, Roland W. Herzog, J. Nathan Hagstrom, +10

Blood

Separation of adeno-associated virus type 2 empty particles from genome containing vectors by anion-exchange column chromatography

Guang Qu, Jennifer Bahr-Davidson, Joseph Prado, +13

Journal of Virological Methods

Virus StructureEmpty ParticlesAnion-exchange Column ChromatographyMolecular BiologyVirology +3

Molecular Cloning and Expression of Mouse Placental Lactogen I Complementary Deoxyribonucleic Acid

Peter Colosi, Frank Talamantes, Daniel I. H. Linzer

Molecular Endocrinology

Coexpression of factor VIII heavy and light chain adeno-associated viral vectors produces biologically active protein

Melissa Burton, Hiroyuki Nakai, Peter Colosi, +3

Proceedings of the National Academy of Sciences

ImmunologyViral PathogenesisMolecular BiologyViral Structural ProteinActive Protein +15

Identification of mouse AAV capsid-specific CD8+ T cell epitopes

Denise E. Sabatino, Federico Mingozzi, Daniel J. Hui, +4

Molecular Therapy