The Antisense Transcript SMN-AS1 Regulates SMN Expression and Is a Novel Therapeutic Target for Spinal Muscular Atrophy

Constantin d’Ydewalle, Daniel M. Ramos, Noah J. Pyles, Shi‐Yan Ng, Mariusz Gorz, Celeste M. Pilato, Karen Ling, Lingling Kong, Amanda J. Ward, Lee L. Rubin,

Neuron · 2016 · 137 citations · 84 references

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