Publication | Open Access
The Antisense Transcript SMN-AS1 Regulates SMN Expression and Is a Novel Therapeutic Target for Spinal Muscular Atrophy
133
Citations
84
References
2016
Year
Musculoskeletal ResearchDegenerative DiseaseNovel Therapeutic TargetSpinal Muscular AtrophyAntisense TherapySystems BiologyCell BiologyGene Expression
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