Concepedia

Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria

Cary O. Harding, Melanie B. Gillingham, Kelly Hamman, Heather D. Clark, E Goebel-Daghighi, Andrew Bird, D.D. Koeberl

Gene Therapy · 2005 · 82 citations · 28 references

DOIFull text

Open access

Concepts

References

28

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

Guangping Gao, Mauricio R. Alvira, Lili Wang et al. · Proceedings of the National Academy of Sciences · 2002 · 1.5K citations · Full text

, , +15

Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction with Broad Specificity

Joseph E. Rabinowitz, Fabienne Rolling, Chengwen Li et al. · Journal of Virology · 2002 · 750 citations · Full text

, , +14

Gene Therapy Vectors Based on Adeno-Associated Virus Type 1

Weidong Xiao, Narendra Chirmule, Scott C. Berta et al. · Journal of Virology · 1999 · 536 citations · Full text

, , +15

Fluorimetric method for the determination of phenylalanine in serum

M. W. McCaman, Eli Robins · Journal of Laboratory and Clinical Medicine · 1962 · 458 citations

, , +2

AAV serotype 2 vectors preferentially integrate into active genes in mice

Hiroyuki Nakai, Eugenio Montini, Sally Fuess et al. · Nature Genetics · 2003 · 394 citations

, , +12