High-resolution insertion-site analysis by linear amplification–mediated PCR (LAM-PCR)

<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1

S. Hacein-Bey-Abina, Christof von Kalle, Manfred Schmidt et al. · Science · 2003 · 3.5K citations

Primary Immunodeficiency, Human Retrovirus, T-regulatory Cell +14

Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease

Marina Cavazzana, Salima Hacein‐Bey, Geneviève de Saint Basile et al. · Science · 2000 · 2.6K citations

Adaptive Immune System, Immunodeficiencies, Immunology +21

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1

Marion Ott, Manfred Schmidt, Kerstin Schwarzwaelder et al. · Nature Medicine · 2006 · 1.2K citations

Gene Therapies, Autoimmune Disease, Novel Therapy +10

Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning

Alessandro Aiuti, Shimon Slavin, Memet Aker et al. · Science · 2002 · 1.1K citations

Cell Therapy, Immunology, Nonmyeloablative Conditioning +17

In Vivo Footprinting of a Muscle Specific Enhancer by Ligation Mediated PCR

Paul R. Mueller, B Wold · Science · 1989 · 962 citations

Muscle Function, Engineering, Cytoskeleton +17