Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats

Juliette Hordeaux, Laurence Dubreil, Johan Deniaud, Fabien Iacobelli, Stéphanie Moreau, Mireille Ledevin, Caroline Le Guiner, Véronique Blouin, Johanne Le Duff, Alexandra Mendes-Madeira,

Gene Therapy · 2015 · 46 citations · 40 references

Concepts

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