Johanne Le Duff

Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy

Caroline Le Guiner, Laurent Servais, Marie Montus et al. · Nature Communications · 2017 · 233 citations · Full text

Medicine, Molecular Medicine, Veterinary Clinical Sciences +17

Forelimb Treatment in a Large Cohort of Dystrophic Dogs Supports Delivery of a Recombinant AAV for Exon Skipping in Duchenne Patients

Caroline Le Guiner, Marie Montus, Laurent Servais et al. · Molecular Therapy · 2014 · 114 citations · Full text

Medicine, Molecular Medicine, Gene Delivery +16

Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats

Juliette Hordeaux, Laurence Dubreil, Johan Deniaud et al. · Gene Therapy · 2015 · 46 citations

Medicine, Neurobiology, Neuroscience +12

Five Years of Successful Inducible Transgene Expression Following Locoregional Adeno-Associated Virus Delivery in Nonhuman Primates with No Detectable Immunity

Mickaël Guilbaud, Marie‐Françoise Devaux, Celia Couzinié et al. · Human Gene Therapy · 2019 · 39 citations · Full text

Pharmacy, Immunology, Molecular Biology +17

Generation and in vivo evaluation of IL10-treated dendritic cells in a nonhuman primate model of AAV-based gene transfer

Aurélie Moreau, Céline Vandamme, Mercedes Segovia et al. · Molecular Therapy — Methods & Clinical Development · 2014 · 24 citations · Full text

Pharmacy, Immunology, Translational Sciences +17