PLoS ONE · 2013 · 378 citations · 27 references
Life SciencesGeneticsMolecular BiologyGenetic EngineeringGenome EditingGenome EngineeringCrispr-based EngineeringCrispr-cas SystemsFish GenomicsMutagenesis StrategiesTarget Site SelectionCas Nuclease EngineeringClustered Regularly Interspaced Short Palindromic Repeats (Crispr)-based MutagenesisCrispr-based Genome EngineeringCrispr-cas Genome EditingCrispr-cas9 Genome EditingGermline TransmissionPrecise Genome EditingSomatic Mutations
A simple, customizable CRISPR‑Cas9 RNA‑guided nuclease system has been shown to efficiently introduce somatic indel mutations in zebrafish genes. The study aims to extend this system to enable precise sequence edits via ssODNs and to broaden its targeting range from 1 in 128 to 1 in 8 base pairs. This is achieved by combining RGN with single‑stranded oligodeoxynucleotides for precise edits and implementing strategies that increase target density. RGN‑induced mutations are heritable with germline transmission efficiencies up to 100%, demonstrating that the system can produce precise, heritable genome modifications in zebrafish.
We have previously reported a simple and customizable CRISPR (clustered regularly interspaced short palindromic repeats) RNA-guided Cas9 nuclease (RGN) system that can be used to efficiently and robustly introduce somatic indel mutations in endogenous zebrafish genes. Here we demonstrate that RGN-induced mutations are heritable, with efficiencies of germline transmission reaching as high as 100%. In addition, we extend the power of the RGN system by showing that these nucleases can be used with single-stranded oligodeoxynucleotides (ssODNs) to create precise intended sequence modifications, including single nucleotide substitutions. Finally, we describe and validate simple strategies that improve the targeting range of RGNs from 1 in every 128 basepairs (bps) of random DNA sequence to 1 in every 8 bps. Together, these advances expand the utility of the CRISPR-Cas system in the zebrafish beyond somatic indel formation to heritable and precise genome modifications.
27
A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial Immunity
Martin Jínek, Krzysztof Chylinski, Ines Fonfara et al. · Science · 2012 · 17.3K citations · Full text
Multiplex Genome Engineering Using CRISPR/Cas Systems
Le Cong, F. Ann Ran, David Cox et al. · Science · 2013 · 15.7K citations
RNA-Guided Human Genome Engineering via Cas9
Prashant Mali, Luhan Yang, Kevin M. Esvelt et al. · Science · 2013 · 9.4K citations · Full text
Efficient genome editing in zebrafish using a CRISPR-Cas system
Woong Y. Hwang, Yanfang Fu, Deepak Reyon et al. · Nature Biotechnology · 2013 · 3K citations · Full text
RNA-guided editing of bacterial genomes using CRISPR-Cas systems
Wenyan Jiang, David Bikard, David Cox et al. · Nature Biotechnology · 2013 · 2.5K citations