Structure-based chemical modification strategy for enzyme replacement treatment of phenylketonuria

Wang Lin, Alejandra Gámez, Christineh N. Sarkissian, Mary Straub, Marianne G. Patch, Gye Won Han, Steve Striepeke, Paul Fitzpatrick, Charles R. Scriver, Raymond C. Stevens

Molecular Genetics and Metabolism · 2005 · 65 citations · 21 references

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