Concepedia

In-frame Dystrophin Following Exon 51-Skipping Improves Muscle Pathology and Function in the Exon 52–Deficient mdx Mouse

Yoshitsugu Aoki, Akinori Nakamura, Toshifumi Yokota, Takashi Saito, Hitoshi Okazawa, Tetsuya Nagata, Shin’ichi Takeda

Molecular Therapy · 2010 · 135 citations · 49 references

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49

Dose translation from animal to human studies revisited

Shannon Reagan‐Shaw, Minakshi Nihal, Nihal Ahmad · The FASEB Journal · 2007 · 6.3K citations

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Dystrophin: The protein product of the duchenne muscular dystrophy locus

Eric P. Hoffman, Robert H. Brown, Louis M. Kunkel · Cell · 1987 · 4.7K citations

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An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus

Anthony P. Monaco, Corlee J. Bertelson, Sabina Liechti‐Gallati et al. · Genomics · 1988 · 1.2K citations

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The molecular basis for Duchenne versus Becker muscular dystrophy: correlation of severity with type of deletion.

Alan H. Beggs, Mary B. Moyer, S. Scherpf et al. · PubMed · 1989 · 961 citations

, , +10

Local Dystrophin Restoration with Antisense Oligonucleotide PRO051

Judith C. van Deutekom, Anneke A. M. Janson, Ieke B. Ginjaar et al. · New England Journal of Medicine · 2007 · 762 citations

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