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Improved Metabolic Correction in Patients with Lysosomal Storage Disease Treated with Hematopoietic Stem Cell Transplant Compared with Enzyme Replacement Therapy

TransplantationMarrow TransplantationEnzyme Replacement TherapyTransplantation MedicineHematologyCell Replacement TherapySubstrate Reduction TherapyMedicineMetabolic CorrectionLysosomal Storage Disease