Jaap Jan Boelens

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Alessandra Biffi, Eugenio Montini, Laura Lorioli et al. · Science · 2013 · 1.2K citations · Full text

Life Sciences, Genetics, Hematology +16

Neutrophils Kill Antibody-Opsonized Cancer Cells by Trogoptosis

Hanke L. Matlung, Liane Babes, Xi Zhao et al. · Cell Reports · 2018 · 391 citations · Full text

Life Sciences, Immunology, Oncology +15

Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: an open-label, phase 3, randomised controlled trial

Selim Corbacioglu, Simone Cesaro, Maura Faraci et al. · The Lancet · 2012 · 375 citations

Medicine, Hematology, Pediatrics +12

Long-term outcome of Hurler syndrome patients after hematopoietic cell transplantation: an international multicenter study

Mieke Aldenhoven, Robert Wynn, Paul J. Orchard et al. · Blood · 2015 · 317 citations · Full text

Medicine, Hematology, Stem Cell Transplantation +15

Defective cytotoxic lymphocyte degranulation in syntaxin-11–deficient familial hemophagocytic lymphohistiocytosis 4 (FHL4) patients

Yenan T. Bryceson, Eva Rudd, Chengyun Zheng et al. · Blood · 2007 · 307 citations · Full text

Medicine, Genetics, Immunology +9