Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)

J. E. Wraith, L. Clarke, Michael Beck, Edwin H. Kolodny, Gregory M. Pastores, Joseph Muenzer, David M. Rapoport, Kenneth I. Berger, Stuart J. Swiedler, Emil Kakkis,

The Journal of Pediatrics · 2004 · 546 citations · 26 references

Concepts

References

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