Publication | Closed Access
Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)
540
Citations
26
References
2004
Year
Enzyme Replacement TherapyRecombinant Human α-L-iduronidasePathologyNeurologyMultinational StudyMedicineLysosomal Storage Disease
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