Sustained correction of OTC deficiency in spfash mice using optimized self-complementary AAV2/8 vectors

Lili Wang, Huan Wang, Hiroki Morizono, Peter Bell, Debra Jones, Julian Lin, D McMenamin, Hongwei Yu, Mark L. Batshaw, James M. Wilson

Gene Therapy · 2011 · 41 citations · 23 references

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