John T. Gray

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

Amit C. Nathwani, Edward G. D. Tuddenham, Savita Rangarajan et al. · New England Journal of Medicine · 2011 · 1.8K citations · Full text

Medicine, Hematology, Molecular Medicine +13

Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2014 · 1.3K citations · Full text

Medicine, Genetics, Molecular Genetics +17

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver

Amit C. Nathwani, John T. Gray, Catherine Y. Ng et al. · Blood · 2005 · 422 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +13

Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins

Amit C. Nathwani, Cecilia Rosales, Jenny McIntosh et al. · Molecular Therapy · 2011 · 350 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +14

Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency

Suk See De Ravin, Xiaolin Wu, Susan Moir et al. · Science Translational Medicine · 2016 · 288 citations · Full text

Medicine, Hematology, Immunology +14